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Important Research Breakthrough
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>From : JulesHoff@aol.com
Date : Sun, 5 Nov 2000 12:02:43 EST
Subject: IMPORTANT RESEARCH BREAKTHROUGH
Julianne Hoffenberg
Co-Founder, Project A.L.S.
Project A.L.S.
FOR IMMEDIATE RELEASE Contact: Patricia Harrington,
212-581-0407
: Nina Capelli, 212-627-2568
TRANSPLANTED NEURAL STEM CELLS RESTORE MOVEMENT
IN PARALYZED MICE
Project A.L.S.-Funded Experiments Are History's
First Involving Stem
Cell Replacement in ALS
(New York, November 5, 2000) Project A.L.S.
and Johns Hopkins University
announced today that after being transplanted
with neural stem cells,
paralyzed mice with an ALS-like syndrome
regained movement. The results
were presented at the annual meeting of The
Society for Neuroscience in
New Orleans, and at Project A.L.S. headquarters
in New York. Project
A.L.S. is the non-profit organization that
has forged and fully funded
Neural Stem Cell Replacement in ALS, a collaborative
investigation uniting
many of the world's leading neuroscientists,
stem cell biologists, and
molecular biologists. The data are a result
of this collaboration.
Johns Hopkins researchers injected the neural
stem cells into the cerebral
spinal fluid of the rodents, which had been
paralyzed as a result of
Sindbis, an animal virus. Sindbis virus approximates
ALS (amyotrophic
lateral sclerosis) in that it selectively
destroys motor neurons, the cells
responsible for movement and breathing. Normally,
Sindbis virus destroys
motor function permanently. But, in the case
of this investigation, over
fifty percent of Sindbis rodents transplanted
with neural stem cells
regained motor function within eight weeks
of the procedure.
The data give further encouragement to scientists
that neural stem cells,
undifferentiated cells possessing the ability
to transform into a range
of healthy new cells, represent potential
treatments and cures for
millions with Alzheimer's, Parkinson's, Huntington's,
spinal muscular
atrophy, stroke and spinal cord injury.
Johns Hopkins neuroscientist, Douglas Kerr,
M.D., Ph.D., the principal
investigator on the Sindbis experiments said,
"This work was driven by the
people at Project A.L.S. with their diligence
and support. It is rare for
a private organization to dramatically reshape
the way research is
pursued. But that has happened here."
Other investigators directly
involved with the Sindbis work were Jeffrey
D. Rothstein, M.D., Ph.D. and
John Gearhart, Ph.D. of Johns Hopkins University,
and Evan Y. Snyder, M.D.,
Ph.D. of Children's Hospital, Boston.
In 1999, Project A.L.S. set out to unite
the world's leading stem cell
biologists with ALS researchers--groups that
had not worked together
before--and charged them with the task of
replacing damaged spinal motor
neurons with stem cells. As a result, research
teams from participating
institutions including Johns Hopkins University,
Children's Hospital,
Boston, Brigham and Women's Hospital, Massachusetts
General Hospital,
Cornell University, and the Howard Hughes
Medical Institute, Columbia
University, have worked together to move
stem cell replacement forward
exponentially.
Jenifer Estess, the 38-year-old president
of Project A.L.S. who is living
with the disease said, "This is the
kind of breakthrough we've been
working toward. Our scientists are our partners
in this fight--we knew
they were applying best efforts to stem cell
replacement in ALS. Project
A.L.S. is thrilled that the mice are walking
again. Now it's time to
give people the same option. I am confident
we'll get there."
Project A.L.S. was founded in 1998, by Ms.
Estess, her family and friends.
Today, Project A.L.S. funds and motivates
investigations including Neural
Stem Cell Replacement in ALS, Genetics, Genomics
& ALS, Rescue of
Respiratory Motor Neurons, High Throughput
Drug Screening, and Accelerated
Drug Testing, among others.
ALS is a fatal neuromuscular disease that
destroys motor neurons, which
control walking talking and breathing. To
date, there is not one
effective treatment for the disease, which
was first described over 150
years ago. The life expectancy for someone
with ALS is two to five years.
Project A.L.S. applies significant funding
to leading scientists, many
of whom have not worked on ALS before, in
the name of understanding the
pathways of the ALS and putting effective
treatments in place as quickly
as possible.